Brazilian Consensus Guidelines for Hematopoietic Stem Cell Transplantation - Inborn errors of metabolismo

Authors

  • Alessandra Araujo Gomes Hospital Sírio-Libanês; ITACI-ICr/HCFMUSP
  • Adriana Mello Rodrigues Hospital Infantil Pequeno Príncipe; Hospital de Clínicas da Universidade Federal do Paraná
  • Juliana Folloni Fernandes Hospital Israelita Albert Einstein; ITACI-ICr/HCFMUSP
  • Liane Daudt Hospital de Clínicas de Porto Alegre; Hospital Moinhos de Vento
  • Carmem Bonfim Hospital Infantil Pequeno Príncipe; Hospital de Clínicas da Universidade Federal do Paraná; Hospital Nossa Senhora das Graças

DOI:

https://doi.org/10.46765/2675-374X.2021v2n4p126

Keywords:

Inborn errors of metabolism, Pediatric patients, Stem cell transplantation

Abstract

Hematopoietic stem cell transplantation (HSCT) has the potential to cure a significant proportion of patients with malignant and nonmalignant diseases. The main rationale for HSCT in inborn errors of metabolism (IEM) is based on correcting the decreases enzymes by the donor cells within and outside the intravascular compartment.

In this article, Brazilian Group for Pediatric Bone Marrow Transplantation of the Brazilian Society of Bone Marrow Transplantation and Cellular Therapy (SBTMO) provides a review of HSCT indications in IEM.

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Published

11/30/2021

How to Cite

Gomes, A. A., Mello Rodrigues, A., Folloni Fernandes, J., Daudt, L., & Bonfim, C. (2021). Brazilian Consensus Guidelines for Hematopoietic Stem Cell Transplantation - Inborn errors of metabolismo. JOURNAL OF BONE MARROW TRANSPLANTATION AND CELLULAR THERAPY, 2(4), 126. https://doi.org/10.46765/2675-374X.2021v2n4p126

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