TY - JOUR AU - Gomes, Alessandra Araujo AU - Mello Rodrigues, Adriana AU - Folloni Fernandes, Juliana AU - Daudt, Liane AU - Bonfim, Carmem PY - 2021/11/30 Y2 - 2024/03/28 TI - Brazilian Consensus Guidelines for Hematopoietic Stem Cell Transplantation - Inborn errors of metabolismo JF - JOURNAL OF BONE MARROW TRANSPLANTATION AND CELLULAR THERAPY JA - jbmtct VL - 2 IS - 4 SE - Original article DO - 10.46765/2675-374X.2021v2n4p126 UR - https://www.jbmtct.com.br/seer/index.php/jbmtct/article/view/126 SP - 126 AB - <p>Hematopoietic stem cell transplantation (HSCT) has the potential to cure a significant proportion of patients with malignant and nonmalignant diseases. The main rationale for HSCT in inborn errors of metabolism (IEM) is based on correcting the decreases enzymes by the donor cells within and outside the intravascular compartment.</p><p>In this article, Brazilian Group for Pediatric Bone Marrow Transplantation of the Brazilian Society of Bone Marrow Transplantation and Cellular Therapy (SBTMO) provides a review of HSCT indications in IEM.</p> ER -